The development of a world-first nasal spray vaccine could be a turning point in protection against whooping cough, helping stop the spread of the respiratory infection to vulnerable babies.

For the first time outside of the United States, doctors in the Kids Cancer Centre at Sydney Children’s Hospital, Randwick (SCH) will use CAR-T cell therapy to try to attack and destroy the fatal tumour, offering new hope to children living with the devastating disease.

New research has shown newborn bloodspot screening is more effective than conventional clinical diagnosis pathways for improving health outcomes in infants with SMA.

Experts are calling for research to look at how gene therapies can be adapted and scaled to become standard practices for people right around Australia.

In a new clinical trial being led by The Children’s Hospital at Westmead, doctors are testing whether drug used to help adult Alzheimer’s patients can help improve some of the devastating features of Rett syndrome.