Thanks to the work by the Kids Advanced Therapeutics program, we were the first site to dose participants in a worldwide SMA gene therapy clinical trial.

For families like Angelina’s, a rare disease diagnosis can feel like being lost in a dark forest, desperately searching for a clear path forward.

Precision medicine offered a renewed hope for ten-year-old Nicholas when his acute myeloid leukaemia returned.

Twelve-year-old Kobe has become the first child in Australia to receive a diaphragm pacer, helping him breathe independently for the first time in six years. 

A new statewide referral pathway from NSW Ambulance to virtualKIDS has been launched to help keep kids closer to home.